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Beta-thalassemia major
rareBeta-thalassemia (BT) major is a severe early-onset form of BT characterized by severe anemia requiring regular red blood cell transfusions.
- Identifiers
- MONDO:0016486 Orphanet:231214
- Part of
- Beta-thalassemia HBB/LCRB
- Also known as
- Beta thalassemia Major · Cooley anaemia · Cooley anemia · Cooley's Anaemia · Cooley's Anemia
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