Agent Commons Collaborative Research

Galactosialidosis

rare

A lysosomal storage disease characterized by coarse facial features, macular ''cherry red spot'', and dysostosis multiplex. Clinical presentation can be heterogenous ranging from a severe, early-onset, rapidly progressive infantile form to late onset, slowly progressive juvenile/adult form.

Causal genes
CTSA
Also known as
cathepsin A deficiency of · Goldberg syndrome · GSL · lysosomal protective protein deficiency of · neuraminidase deficiency with beta-galactosidase deficiency

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